Articles in Journal
2022
Lederer C.W, Koniali L, Buerki-Thurnherr T, Papasavva P.L, La Grutta S, Licari A, Staud F, Bonifazi D, Kleanthous M.
Pharmaceutics 2022, 14, 793. doi.org/10.3390/
2021
Medical Device Development for Children and Young People—Reviewing the Challenges and Opportunities
P. Dimitri, V. Pignataro, M. Lupo, D. Bonifazi , M. Henke , U. M. Musazzi, F. Ernst, P. Minghetti, D. F. Redaelli, S. G. Antimisiaris, G. Migliaccio, F. Bonifazi, L. Marciani, A. J. Courtenay, N. Denora, A. Lopedota
Pharmaceutics 2021, 13(12), 2178; https://doi.org/10.3390/pharmaceutics13122178
________________
The GluN2B-Selective Antagonist Ro 25-6981 Is Effective
P. Mareš, L. Kozlová , A. Mikulecká, H. Kubová
Pharmaceutics 2021, 13, 1482; https://doi.org/10.3390/pharmaceutics13091482
________________
Children’s Preferences for Oral Dosage Forms and Their Involvement in Formulation Research via EPTRI (European Paediatric Translational Research Infrastructure)
E. Alessandrini, F. Brako, M. Scarpa, M. Lupo , D. Bonifazi, V. Pignataro, M. Cavallo, O. Cullufe, C. Enache, B. Nafria, J. Claverol, L. De Taeye, E. Vermeulen, J. Preston, C. Tuleu
Pharmaceutics 2021, 13, 730; https://doi.org/10.3390/pharmaceutics13050730
Detection of Breathing Movements of Preterm Neonates by Recording Their Abdominal Movements with a Time-of-Flight Camera
F. C. Wiegandt, D. Biegger , J. F. Fast, G. Matusiak, J. Mazela, T. Ortmaier, T. Doll, A. Dietzel, B. Bohnhorst, G. Pohlmann
Pharmaceutics 2021, 13, 721; https://doi.org/10.3390/pharmaceutics13050721
________________
Drug Safety in Translational Paediatric Research: Practical Points to Consider for Paediatric Safety Profiling and Protocol Development: A Scoping Review
B. Aurich, E. Jacqz-Aigrain
Pharmaceutics 2021, 13, 695; https://doi.org/10.3390/pharmaceutics13050695
________________
Breath-Triggered Drug Release System for Preterm Neonates
F. C. Wiegandt, U. P. Froriep, F. Müller, T. Doll, A. Dietzel, G. Pohlmann
Pharmaceutics 2021, 13, 657; https://doi.org/10.3390/pharmaceutics13050657
________________
Human Microbiome in Children, at the Crossroad of Social Determinants of Health and Personalized Medicine
Talía Sainz, Valeria Pignataro, Donato Bonifazi, Simona Ravera, María José Mellado, Antonio Pérez-Martínez , Adela Escudero, Adriana Ceci and Cristina Calvo
Children 2021, 8, 1191; https://doi.org/10.3390/children8121191
________________
The Neonatal and Juvenile Pig in Pediatric Drug Discovery and Development
M. Ayuso, L. Buyssens, M. Stroe, A. Valenzuela, K. Allegaert, A. Smits, P. Annaert, A. Mulder, S. Carpentier, C. Van Ginneken, S. Van Cruchten
Pharmaceutics 2021, 13/3; doi: 10.3390/pharmaceutics13030415
________________
Patient-Derived Induced Pluripotent Stem Cells (iPSCs) and Cerebral Organoids for Drug Screening and Development in Autism Spectrum Disorder: Opportunities and Challenges
C. Villa, R. Combi, D. Conconi, M. Lavitrano
Pharmaceutics 2021, 13/2; doi: 10.3390/pharmaceutics13020280
________________
2020
Ethical, Legal and Regulatory Issues of Paediatric Translational Research. Call for an Adequate Model of Governance
A. Altavilla, V. Giannuzzi, M. Lupo, D. Bonifazi, A. Ceci
European Journal of Health Law 2020, May 18; doi: 10.1163/15718093-bja10010
________________
Pediatric Biobanking: Kids Are Not Just Little Adults
D. R. Catchpoole, D. Carpentieri, S. Vercauteren, L. Wadhwa, W. Schleif, L. Zhou, J. Zhou, R. M. Labib, E. Smits, E. H. Conradie
Biopreservation and Biobanking 18/4, 2020, August; doi: 10.1089/bio.2020.29071.djc
________________
Chapter in book
Challenges and New Frontiers in the Paediatric Drug Discovery and Development
A. Intini, D. Bonifazi, G. Migliaccio
Drug Discovery and Development – New Advances, 2019; 10.5772/intechopen.85635
EPTRI Special Issues
Special Issue dedicated to the Scientific Highlights in the European Paediatric Translational Research Infrastructure has been published into the section “Drug Delivery and Controlled Release” of the Pharmaceutics Journal at the end of 2021.
The Special Issue has been addressed to all researchers and partners involved in the development of paediatric medicines working on the following topics: i) paediatric medicines drug targets and methods of identification; ii) advanced cellular/in vitro models for paediatric drug targeting; iii) paediatric formulations and toxicology of drugs; iv) drug delivery design in paediatrics; v) translational research.
The EPTRI members published 12 articles in this Special Issue.
- In Vivo Investigation of (2-Hydroxypropyl)-β-cyclodextrin-Based Formulation of Spironolactone in Aqueous Solution for Paediatric Use, Antonio Lopalco, Annachiara Manni, Alexander Keeley, Shozeb Haider, Wenliang Li, Angela Lopedota, Cosimo Damiano Altomare, Nunzio Denora, Catherine Tuleu. Pharmaceutics 2022, 14(4), 780; https://doi.org/10.3390/pharmaceutics14040780
- Intestinal Cellular Biomarkers of Mucosal Lesion Progression in Pediatric Celiac Disease, Serena Vitale, Mariantonia Maglio, Stefania Picascia, Ilaria Mottola, Erasmo Miele, Riccardo Troncone, Renata Auricchio, Carmen Gianfrani. Pharmaceutics 2021, 13(11), 1971; https://doi.org/10.3390/pharmaceutics13111971
- N2B-Selective Antagonist Ro 25-6981 Is Effective against PTZ-Induced Seizures and Safe for Further Development in Infantile Rats, Pavel Mareš, Lucie Kozlová, Anna Mikulecká, Hana Kubová. Pharmaceutics 2021, 13(9), 1482; https://doi.org/10.3390/pharmaceutics13091482
- Children’s Preferences for Oral Dosage Forms and Their Involvement in Formulation Research via EPTRI (European Paediatric Translational Research Infrastructure), Elisa Alessandrini, Francis Brako, Mariagiovanna Scarpa, Mariangela Lupo, Donato Bonifazi, Valeria Pignataro, Maria Cavallo, Ornela Cullufe, Cristina Enache, Begonya Nafria, Joana Claverol, Leen De Taeye, Eric Vermeulen, Jennifer Preston, Catherine Tuleu. Pharmaceutics 2021, 13(5), 730; https://doi.org/10.3390/pharmaceutics13050730
- Detection of Breathing Movements of Preterm Neonates by Recording Their Abdominal Movements with a Time-of-Flight Camera, Felix C. Wiegandt, David Biegger, Jacob F. Fast, Grzegorz Matusiak, Jan Mazela, Tobias Ortmaier, Theodor Doll, Andreas Dietzel, Bettina Bohnhorst, Gerhard Pohlmann. Pharmaceutics 2021, 13(5), 721; https://doi.org/10.3390/pharmaceutics13050721
- Breath-Triggered Drug Release System for Preterm Neonates, Felix C. Wiegandt, Ulrich P. Froriep, Fabian Müller, Theodor Doll, Andreas Dietzel, Gerhard Pohlmann. Pharmaceutics 2021, 13(5), 657; https://doi.org/10.3390/pharmaceutics13050657
- Anticonvulsant Action of GluN2A-Preferring Antagonist PEAQX in Developing Rats, Pavel Mares, Grygoriy Tsenov, Hana Kubova. Pharmaceutics 2021, 13(3), 415; https://doi.org/10.3390/pharmaceutics13030415
- Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies, Carsten W. Lederer, Lola Koniali, Tina Buerki-Thurnherr, Panayiota L. Papasavva, Stefania La Grutta, Amelia Licari, Frantisek Staud, Donato Bonifazi, Marina Kleanthous. Pharmaceutics 2022, 14(4), 793; https://doi.org/10.3390/pharmaceutics14040793
- Medical Device Development for Children and Young People—Reviewing the Challenges and Opportunities, Paul Dimitri, Valeria Pignataro, Mariangela Lupo, Donato Bonifazi, Maria Henke, Umberto M. Musazzi, Floris Ernst, Paola Minghetti, Davide F. Redaelli, Sophia G. Antimisiaris, Giovanni Migliaccio, Fedele Bonifazi, Luca Marciani, Aaron J. Courtenay, Nunzio Denora, Angela Lopedota. Pharmaceutics 2021, 13(12), 2178; https://doi.org/10.3390/pharmaceutics13122178
- Drug Safety in Translational Paediatric Research: Practical Points to Consider for Paediatric Safety Profiling and Protocol Development: A Scoping Review, Beate Aurich, Evelyne Jacqz-Aigrain. Pharmaceutics 2021, 13(5), 695; https://doi.org/10.3390/pharmaceutics13050695
- Patient-Derived Induced Pluripotent Stem Cells (iPSCs) and Cerebral Organoids for Drug Screening and Development in Autism Spectrum Disorder: Opportunities and Challenges, Chiara Villa, Romina Combi, Donatella Conconi, Marialuisa Lavitrano. Pharmaceutics 2021, 13(2), 280; https://doi.org/10.3390/pharmaceutics13020280
- The Neonatal and Juvenile Pig in Pediatric Drug Discovery and Development, Miriam Ayuso, Laura Buyssens, Marina Stroe, Allan Valenzuela, Karel Allegaert, Anne Smits, Pieter Annaert, Antonius Mulder, Sebastien Carpentier, Chris Van Ginneken, Steven Van Cruchten. Pharmaceutics 2021, 13(1), 44; https://doi.org/10.3390/pharmaceutics13010044